Filter
Survival analysis in untreated patients with thymidine kinase 2 deficiency (TK2d) aged ≤12 years at TK2d symptom onset: findings from the largest international TK2d dataset
Patients' lived experience of thymidine kinase 2 deficiency (TK2d): results from the Assessment of TK2d Patient Perspectives (ATP) study
Survival analyses in patients with thymidine kinase 2 deficiency aged ≤12 years at symptom onset who received pyrimidine nucleos(t)ide therapy
Functional outcomes in patients with thymidine kinase 2 deficiency aged ≤12 years at symptom onset who received pyrimidine nucleos(t)ide therapy
Functional outcomes in untreated patients with thymidine kinase 2 deficiency (TK2d) aged ≤12 years at TK2d symptom onset: findings from the largest international TK2d dataset
Using the Genomics England National Genomic Research Library (NGRL) and UK Biobank to investigate the genetic, phenotypic and clinical landscape of thymidine kinase 2 deficiency (TK2d)
Safety, Tolerability, Pharmacokinetics, and Efficacy of Fenfluramine in Combination With Cannabidiol: Results From an Exploratory Phase 1 Study
Non-seizure benefits of long-term fenfluramine treatment in pediatric patients with Dravet syndrome
Fenfluramine Efficacy Trajectories in Placebo or Treatment Groups From Randomized Controlled Trial to Open-Label Extension in Patients With Lennox-Gastaut Syndrome
Onset and Duration of Adverse Events in Patients Treated With Fenfluramine in the Lennox-Gastaut Syndrome Clinical Trials
Safety and Effectiveness of Fenfluramine for the Treatment of Seizures in Lennox-Gastaut Syndrome: Results From the Final Analysis of an Open-Label Extension Study
Prospective evaluation of non-seizure benefits related to treatment with fenfluramine in pediatric and adult patients with Dravet syndrome
Antiseizure Medication Regimen Adjustment After Fenfluramine Initiation: Lessons Learned From European Early Access Program in Pediatric and Adult Patients With Dravet Syndrome
Use of Fenfluramine and Cannabidiol in Daily Practice: A Retrospective Analysis of German Prescription Claims
Brivaracetam Adjunctive Therapy in Paediatric and Adult Patients With Focal-Onset Seizures in Mid-European Countries: 12-Month, Real-World Outcomes From the BRIVA-REG Study